Several treatments to correct serious genetic disorders will be approved by medical regulators in 2022, and others are producing impressive clinical trial results.
health
December 23, 2022
Gene replacement therapy replaces DNA that is not functioning properly. Shutterstock/SWK Stock
This year has been full of good news about gene replacement therapies that alleviate severe genetic diseases in children.
“We’re curing deadly diseases in children. It’s amazing,” said Donald Cohn of the University of California, Los Angeles. new scientist in May after successfully using gene replacement therapy to reverse a rare, life-threatening immune condition called leukocyte adhesion deficiency in nine children.
Gene replacement therapy is used to correct…
